Niemann-Pick Disease, A Pipeline Analysis Report 2018

Technavio has published a new report on the drug development pipeline for Niemann-pick disease, including a study of the pipeline molecules.

Metabolic Therapeutics - Pharma Proff

Research Updates Archives - The CATS Foundation

Rapid Diagnosis of 83 Patients with Niemann Pick Type C Disease and Related Cholesterol Transport Disorders by Cholestantriol Screening - eBioMedicine

Full article: Current advancements in therapy for Niemann-Pick disease: progress and pitfalls

Investigation of Brain Iron in Niemann-Pick Type C: A 7T Quantitative Susceptibility Mapping Study

MRx Pipeline July 2023 by Magellan Rx Management - Issuu

Insects, Free Full-Text

Precision health in Alzheimer disease: Risk assessment‐based strategies - Azar - 2021 - Precision Medical Sciences - Wiley Online Library

Biomolecules, Free Full-Text

PPT - Acid Sphingomyelinase Deficiency Pipeline Review, H1 2015 PowerPoint Presentation - ID:7149397

Signatures of natural selection and ethnic-specific prevalence of NPC1 pathogenic mutations contributing to obesity and Niemann–Pick disease type C1

Cells, Free Full-Text