Marta, with Niemann Pick C, fights for a cure with gene therapy

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Last updated 03 janeiro 2025
Marta, with Niemann Pick C, fights for a cure with gene therapy
Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease
Marta, with Niemann Pick C, fights for a cure with gene therapy
2017 ACVIM Forum Research Report Program - 2017 - Journal of
Marta, with Niemann Pick C, fights for a cure with gene therapy
Marta – Columbus Children's Foundation
Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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Marta, with Niemann Pick C, fights for a cure with gene therapy
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