Marta, with Niemann Pick C, fights for a cure with gene therapy
Por um escritor misterioso
Last updated 02 fevereiro 2025
Marta is a four and a half year old girl with Niemann Pick C. This is a rare neurodegenerative genetic disease
2017 ACVIM Forum Research Report Program - 2017 - Journal of
Marta – Columbus Children's Foundation
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