TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Children with Niemann-Pick Type C (NPC), their parents and scientists seeking a treatment for this fatal genetic disease. WSJ follows this 6-year fight.

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TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Topic · Rare disease ·

March 2022 – NNPDF

TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

Your Impact - Ara Parseghian Medical Research Fund