Treating Niemann-Pick Disease Type C

Parents of kids with Niemann Pick C advocate for adrabetadex

Miglustat in Niemann-Pick disease type C patients: a review, Orphanet Journal of Rare Diseases

Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC) - The Children's Inn at NIH

Rare Diseases Research: Clinical Trial for Niemann-Pick Type C

Anesthetic consideration of Niemann-Pick Disease type C

Therapeutic intervention for Niemann–Pick type C disease must target

Immune dysfunction in Niemann‐Pick disease type C - Platt - 2016 - Journal of Neurochemistry - Wiley Online Library

Rapid Diagnosis of 83 Patients with Niemann Pick Type C Disease and Related Cholesterol Transport Disorders by Cholestantriol Screening - eBioMedicine

Niemann–Pick type C Mnemonic

Impaired Autophagy in the Lipid-Storage Disorder Niemann-Pick Type C1 Disease - ScienceDirect