CRISPR-Cas9: A method for establishing rat models of drug metabolism and pharmacokinetics - ScienceDirect

Potential disease-modifying therapies for Huntington's disease: lessons learned and future opportunities - The Lancet Neurology

Progress in the application of exosomes as therapeutic vectors in tumor-targeted therapy - Cytotherapy

Gene editing of hematopoietic stem cells restores T-cell response in familial hemophagocytic lymphohistiocytosis - Journal of Allergy and Clinical Immunology

Morquio Syndrome (Mucopolysaccharidosis Type IV) Treatment & Management: Approach Considerations, Medical Care, Surgical Care

Therapies targeting DNA and RNA in Huntington's disease - The Lancet Neurology

Brain organoid: a 3D technology for investigating cellular composition and interactions in human neurological development and disease models in vitro, Stem Cell Research & Therapy

Implementing genome-driven personalized cardiology in clinical practice - Journal of Molecular and Cellular Cardiology

Localized immunomodulation technologies to enable cellular and organoid transplantation: Trends in Molecular Medicine

RNA editing: Expanding the potential of RNA therapeutics: Molecular Therapy