CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular Therapy - Nucleic Acids
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Last updated 08 fevereiro 2025
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CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease
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Functional genomics and the future of iPSCs in disease modeling
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Characterisation of a novel OPA1 splice variant resulting in
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PDF) Establishing induced pluripotent stem cell lines from two
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Retinal Ganglion Cells in a Dish: Current Strategies and
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CRISPR-AsCas12a Efficiently Corrects a GPR143 Intronic Mutation in
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