Treatment Options for Niemann-Pick Type C

Elizabeth Berry-Kravis, MD, PhD, co-director of the Molecular Diagnostics Section of the Genetic Laboratory at Rush Medical College in Chicago, describes dif

Niemann Pick Disease - an overview

Niemann-Pick type C: contemporary diagnosis and treatment of a classical disorder

The pathogenesis of Niemann–Pick type C disease: a role for autophagy?, Expert Reviews in Molecular Medicine

Niemann–Pick Disease Type C

Mitochondrial GSH replenishment as a potential therapeutic approach for Niemann Pick type C disease - ScienceDirect

The pathogenesis of Niemann–Pick type C disease: a role for autophagy?, Expert Reviews in Molecular Medicine

mRNA Treatment Rescues Niemann-Pick Disease Type C1 in Patient Fibroblasts

Niemann-Pick disease type C as a neurovisceral disease. Schematic

Combination therapy a potential strategy for treating Niemann-Pick disease

Main therapies and point of action in Niemann type C disease.

Niemann- Pick Disease Type C (NPC) Market Report 2023-2033 - Wissen Research

Adult Onset Niemann-Pick type C (NPC) – NNPDF